Workpackages

WP n° WP title WPL WPL name WPL short name Other partners involved
1 Pathogenesis and pathophysiology of lysosomal storage diseases >> P2 A. Ballabio FTELE.IGM DPFII
EMC
2 Natural history of lysosomal diseases and enzyme replacement therapy >> P3 A. J.J. Reuser EMC JOGU
DPFII
UCAM
3 Enzyme enhancement by pharmacological chaperones in Pompe disease >> P1 G. Andria DPFII FTELE.IGM
EMC
4 Substrate reduction therapy >> P4 T. Cox UCAM FTELE.IGM
ULUND
5 Gene therapy of animal models of lysosomal storage diseases >> P2 A. Ballabio FTELE.IGM DPFII
ULUND
6 Management of the EUCLYD consortium >> P1 G. Andria DPFII FTELE.IGM